资讯

Muscular Dystrophy News13 小时

I’m waving goodbye to acting, but I’m not about to exit the stage

Columnist Shalom Lim will continue to pursue the themes that matter to him as a person with Duchenne MD, but as a writer now, ...
Muscular Dystrophy News1 天

Early data for experimental DM1 therapy SRP-1003 coming soon

Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Muscular Dystrophy News6 天

Turkish company to sell Duchenne MD steroid therapy Agamree

Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.